Solid Biosciences (SLDB) stock rises as a Phase 1/2 trial for its lead asset SGT-003 in Duchenne muscular dystrophy reaches ...

"New study uncovers key insights into protein interactions in Duchenne muscular dystrophy, paving way for more targeted therapies." ScienceDaily. www.sciencedaily.com / releases / 2024 / 12 / ...

Gene therapy may have the potential to cure Duchenne muscular dystrophy, but early results from clinical trials have not been as promising as researchers hoped. Research is ongoing. Duchenne muscular ...

NEW YORK (AP) — Shares of Sarepta Therapeutics Inc. nearly tripled in value Wednesday after the company reported positive clinical data for its Duchenne muscular dystrophy drug eteplirsen. Sarepta ...

We were unable to process your request. Please try again later. If you continue to have this issue please contact [email protected]. Back to Healio A clinical-stage RNA medicines firm has ...

Your muscles need continuous maintenance to stay strong and healthy. Duchenne muscular dystrophy (DMD) happens when there is a change in a person's genetic instructions that affects the production of ...

Additional analyses from the givinostat clinical development program review observations on weight-based flexible dosing, characterization of thrombocytopenia, correlations between pharmacodynamic ...

A recent study has found that the SMCHD1 protein plays a key role in controlling how genes are processed, which affects the progression of Facioscapulohumeral Muscular Dystrophy (FSHD). This discovery ...

BOULDER, Colo.--(BUSINESS WIRE)--Edgewise Therapeutics, Inc. (Nasdaq: EWTX), a leading muscle disease biopharmaceutical company, today announced the start of enrollment of GRAND CANYON, a global ...

Entrada Therapeutics plans to start ELEVATE-45-201, a Phase 1/2 DMD clinical trial, in Q3 2025 following EU authorization. Entrada Therapeutics, Inc. announced that it will initiate the ELEVATE-45-201 ...

Take advantage of TipRanks Premium at 50% off! Unlock powerful investing tools, advanced data, and expert analyst insights to help you invest with confidence. Medpace Holdings Inc. and Edgewise ...