Astellas Gene Therapies remains intent on treating X-linked Myotubular Myopathy (XLMTM) through a gene therapy—but instead of AAV-based resamirigene bilparvovec (AT132), Astellas is now partnering ...

ELRIG, a not-for-profit, volunteer-led organisation dedicated to the global drug discovery community, today announced the ...

A patient death in a CRISPR trial halts gene editing studies, raising critical safety questions. What this means for the ...

Gene therapy advancements necessitate improved delivery infrastructure and comprehensive data collection across age groups to address logistical complexities and policy gaps. Multidisciplinary ...

Ocugen, Inc. gene therapy outlook: key 2026 catalysts, Phase 2/3 eye-disease data, BLA plans to 2028, and risks. Click for ...

The cell and gene therapy market is at a pivotal point, with a surge in approvals and a maturing pipeline. While oncology remains a stronghold, diversification into other therapeutic areas is ...

There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University’s College of Medicine and the UMass Chan Medical School have achieved ...

Cell and gene therapies use the body's building blocks - cells and genetic material - to boost the immune system or correct ...

As we continue our series exploring genetic medicine, both in this story and in Destiny's Child No Longer: Rewriting Genetic Fate, gene therapy stands at a crossroads. On June 16, Sarepta Therapeutics ...

Cell and gene therapy are revolutionary approaches to treating diseases at the molecular level. They involve the manipulation ...